Liver directed / Rare diseases | Research | IND-Enabling | Phase 1/2 | Phase 3 |
---|---|---|---|---|
FVII deficiency | ||||
FX deficiency | ||||
Hemophilia A | ||||
Two undisclosed programs |
CNS diseases | Research | IND-Enabling | Phase 1/2 | Phase 3 |
---|---|---|---|---|
One undisclosed program |
Liver directed / Rare diseases | Research | IND-Enabling | Phase 1/2 | Phase 3 |
---|---|---|---|---|
FVII deficiency | ||||
FX deficiency | ||||
Hemophilia A | ||||
Two undisclosed programs |
CNS diseases | Research | IND-Enabling | Phase 1/2 | Phase 3 |
---|---|---|---|---|
One undisclosed program |